Search Constraints
Search Results
Select an image to start the slideshow
Gene-based neuromodulation for sustained botulinum toxin expression in the treatment of muscle spasticity: a proof of principle study
1 of 6
Development of a responsive gene therapy to promote clearance of polyglutamine aggregates
2 of 6
Engineering novel chimeric antigen receptors (CARs) for T-cell malignancies using innate immune cells
3 of 6
ATF4-Controlled BECN1 Vectors for Treatment of Huntington’s Disease in R6/2 Mice
4 of 6
Pharmacological analysis of liver-directed AAV-fVIII gene therapy and anti-fVIII inhibitor incidence in a preclinical model of hemophilia A
5 of 6
Brain GALT restoration by intrathecal injection of scAAV9-hGALT enables partial metabolic correction in adolescent GALT-null rats
6 of 6