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Keyword
Classic Galactosemia
3
Classic galactosemia
3
Drosophila
3
Galactosemia
3
galactosemia
2
AAV Gene Therapy
1
AAV8
1
Drosophila development
1
Drosophila melanogaster
1
Duarte galactosemia
1
GALE deficiency
1
Galactose metabolism
1
Gene Therapy
1
Gene therapy
1
Growth
1
Long-Term Outcomes
1
N314D
1
Rat Model
1
UDP-sugars
1
ataxia
1