Antiviral characterization and Anti-reactivation properties of pyrrolopyridine based ALLINIs STP0404 and EKC110

Ancestral Sequence Reconstruction as a Lead Optimization Approach in Gene Therapy Drug Development

The development and functional testing of cellular therapies against protein tyrosine kinase 7 (PTK7) to treat high-risk neuroblastoma

Pharmacological analysis of liver-directed AAV-fVIII gene therapy and anti-fVIII inhibitor incidence in a preclinical model of hemophilia A

Non-genotoxic anti-CD117 conditioning for hematopoietic stem cell transplantation and gene therapy applications

Developing novel cellular and gene therapies for pediatric malignancies